Presentations
Anne Pariser, MD - An Introduction To Preclinical Therapeutics Development
Adam L. Hartman, MD, FAAP, FAAN, FANA, FAES - Clinical Trials 101
Steven L. Roberds, PhD - The Power of Community: Clinical Trial Experience in Tuberous Sclerosis Complex
Tools And Resources
ClinicalTrials.gov - Find out if there are or have been any Clinical Trials for your disorder or related co-morbidities
NCATSToolkit for Patient-focused Therapeutics Development
RaDaR - Rare Diseases Registry Program
Articles
Will add relevant materials as available.
If you have a suggested article, please contact us.